Thank you for supporting Families of Spinal Muscular Atrophy. Because of your commitment to our mission, we are making tremendous strides towards a world where SMA is treatable and curable.
FMSA has made significant progress in advancing new therapies for SMA, starting with funding the first ever SMA drug program in 2000. Now, the time is right for us to build on our success, broad our research, and launch the next phase of therapeutic development work for SMA. FMSA is aiming to fund two new preclinical drug development programs in 2011, with more to follow. These multi-million dollar collaborations will focus on innovative methods of developing novel therapies for SMA, including both biologic and small molecule approaches. Having multiple “shots on goal” gives us the best potential for reaching our objective of a treatment and cure for SMA.